Community Perspectives on Treatment
Our Family’s Experience with Bone Marrow Transplant Treatment
Hello Morquio community! My 8yo son just completed hematopoietic stem cell transplant* (HSCT) to resolve his enzyme deficiency that was brought on by MPS IVA, Morquio Syndrome. This treatment for Morquio was the 2nd treatment of its kind in the US and I wanted to share our story. I wanted to Read more…
